269th ENMC international workshop: 10 years of clinical trials in Duchenne muscular dystrophy – What have we learned? 9–11 December 2022, Hoofddorp, The Netherlands

The 269th ENMC workshop was held from the 9th to the 11th of December 2022 and brought together 24 representatives from all stakeholder groups that have sought to advance development of new therapeutics in clinical trials in Duchenne muscular dystrophy (DMD), including patients, advocacy groups, researchers, regulators and trial sponsors, and neuromuscular and clinical experts from 5 European countries (Belgium, France, Italy, Netherlands and the UK) and from the United States. The workshop was organised by N.

Source: Neuromuscular Disorders - October 10, 2023 Category: Neurology Authors: Karin J. Naarding, Georgia Stimpson, Susan J. Ward, Nathalie Goemans, Craig McDonald, Eugenio Mercuri, Francesco Muntoni, 269th ENMC workshop participants Source Type: research