Development and pilot validation of a novel disfigurement severity scale for plexiform neurofibromas in children with neurofibromatosis type 1
CONCLUSION: This study demonstrates that our observer-rated disfigurement severity score for plexiform neurofibroma was feasible, reliable, and documented improvement in disfigurement in participants with plexiform neurofibroma shrinkage. Prospective studies in larger samples are needed to validate this scale further.PMID:37877369 | DOI:10.1177/17407745231206402
Source: Clinical Trials - Category: Research Authors: Liny John Gurbani Singh Eva Dombi Pamela L Wolters Staci Martin Andrea Baldwin Seth M Steinberg Jessica Bernstein Patricia Whitcomb Dominique C Pichard Anne Dufek Andy Gillespie Kara Heisey Miriam Bornhorst Michael J Fisher Brian D Weiss AeRang Kim Brigit Source Type: research
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