Multifaceted Approach for Quantification and Enzymatic Activity of Iduronate-2-Sulfatase to Support Developing Gene Therapy for Hunter  Syndrome

In conclusion, the multifaceted bioanalytical method for I2S and its enzymatic activity were established to assess gene therapy products in Hunter syndrome.Graphical abstract
Source: The AAPS Journal - Category: Drugs & Pharmacology Source Type: research