Inclusion-Body Myositis Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.
Hereditary Inclusion Body Myopathy-Disease Monitoring (HIBM-DMP): A Combined Registry and Prospective Observational Natural History Study to Assess HIBM Disease
Conditions: Hereditary Inclusion Body Myopathy; GNE Myopathy; Nonaka Disease; Quadriceps Sparing Myopathy (QSM); Distal Myopathy With Rimmed Vacuoles (DMRV)Intervention: Sponsors: Ultragenyx Pharmaceutical Inc; TREAT-NMDRecruiting - verified September 2013 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 4, 2013 Category: Research Source Type: clinical trials
Phase I Clinical Trial of ManNAc in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)
Conditions: Hereditary Inclusion Body Myopathy (HIBM); GNE MyopathyIntervention: Drug: ManNAcSponsors: National Human Genome Research Institute (NHGRI); National Center for Advancing Translational Science (NCATS); Therapeutics for Rare and Neglected Diseases (TRND)Completed - verified March 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 3, 2012 Category: Research Source Type: clinical trials
Follistatin Gene Transfer to Patients With Becker Muscular Dystrophy and Sporadic Inclusion Body Myositis
Conditions: Becker Muscular Dystrophy; Sporadic Inclusion Body MyositisIntervention: Biological: rAAV1.CMV.huFollistatin344Sponsors: Nationwide Children's Hospital; Parent Project Muscular Dystrophy; The Myositis Association (Grant Sponsor)Enrolling by invitation - verified February 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 23, 2012 Category: Research Source Type: clinical trials
A Natural History Study of Patients With Hereditary Inclusion Body Myopathy
Condition: Hereditary Inclusion Body MyopathyIntervention: Sponsors: National Human Genome Research Institute (NHGRI); Therapeutics for Rare and Neglected Diseases (TRND)Recruiting - verified April 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 13, 2011 Category: Research Source Type: clinical trials