Hereditary Inclusion Body Myopathy-Disease Monitoring (HIBM-DMP): A Combined Registry and Prospective Observational Natural History Study to Assess HIBM Disease
Conditions: Hereditary Inclusion Body Myopathy; GNE Myopathy; Nonaka Disease; Quadriceps Sparing Myopathy (QSM); Distal Myopathy With Rimmed Vacuoles (DMRV)Intervention: Sponsors: Ultragenyx Pharmaceutical Inc; TREAT-NMDRecruiting - verified September 2013
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials