Hereditary Inclusion Body Myopathy-Disease Monitoring (HIBM-DMP): A Combined Registry and Prospective Observational Natural History Study to Assess HIBM Disease

Conditions:   Hereditary Inclusion Body Myopathy;   GNE Myopathy;   Nonaka Disease;   Quadriceps Sparing Myopathy (QSM);   Distal Myopathy With Rimmed Vacuoles (DMRV)Intervention:   Sponsors:   Ultragenyx Pharmaceutical Inc;   TREAT-NMDRecruiting - verified September 2013
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials