Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)
Conditions:   Hereditary Inclusion Body Myopathy;   Distal Myopathy With Rimmed Vacuoles;   Distal Myopathy, Nonaka TypeInterventions:   Drug: Sialic Acid Tablets;   Drug: Placebo TabletsSponsor:   Ultragenyx Pharmaceutical IncNot yet recruiting - verified May 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 27, 2015 Category: Research Source Type: clinical trials

Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)
Conditions:   Hereditary Inclusion Body Myopathy;   Distal Myopathy With Rimmed Vacuoles;   Distal Myopathy, Nonaka TypeInterventions:   Drug: Sialic Acid Tablets;   Drug: Placebo TabletsSponsor:   Ultragenyx Pharmaceutical IncNot yet recruiting - verified April 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 27, 2015 Category: Research Source Type: clinical trials

Blood-flow Restricted Exercise in Inclusion Body Myositis
Condition:   Sporadic Inclusion Body MyositisInterventions:   Other: Blood-flow restricted training;   Drug: Care as usualSponsors:   University of Southern Denmark;   Odense University HospitalActive, not recruiting - verified March 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 10, 2014 Category: Research Source Type: clinical trials

Clinical, Biological and NMR Outcome Measures Study for Hereditary Inclusion Body Myopathy Due to Mutation of UDP-N-acetylglucosamine 2-epimerase/N-acetylmannosamine Kinase Gene (GNE)
Condition:   HIBMInterventions:   Other: motor function and strength assessment;   Other: NMR assessment;   Other: 24h urine and serum collectionSponsor:   Institut de Myologie, FranceRecruiting - verified April 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 8, 2014 Category: Research Source Type: clinical trials