Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)
Conditions: Hereditary Inclusion Body Myopathy; Distal Myopathy With Rimmed Vacuoles; Distal Myopathy, Nonaka TypeInterventions: Drug: Sialic Acid Tablets; Drug: Placebo TabletsSponsor: Ultragenyx Pharmaceutical IncNot yet recruiting - verified May 2015
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials