Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)

Conditions:   Hereditary Inclusion Body Myopathy;   Distal Myopathy With Rimmed Vacuoles;   Distal Myopathy, Nonaka TypeInterventions:   Drug: Sialic Acid Tablets;   Drug: Placebo TabletsSponsor:   Ultragenyx Pharmaceutical IncNot yet recruiting - verified May 2015
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials