Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
Conditions:   Fanconi Anemia Complementation Group A;   Fanconi Anemia Intervention:   Other: Safety and efficacy assessments Sponsor:   Rocket Pharmaceuticals Inc. Enrolling by invitation (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 19, 2020 Category: Research Source Type: clinical trials

Gene Therapy for Fanconi Anemia, Complementation Group A
Condition:   Fanconi Anemia Complementation Group A Intervention:   Biological: RP-L102 Sponsor:   Rocket Pharmaceuticals Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 30, 2020 Category: Research Source Type: clinical trials