Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
Conditions: Fanconi Anemia Complementation Group A; Fanconi Anemia Intervention: Other: Safety and efficacy assessments Sponsor: Rocket Pharmaceuticals Inc. Enrolling by invitation (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 19, 2020 Category: Research Source Type: clinical trials
Gene Therapy for Fanconi Anemia, Complementation Group A
Condition: Fanconi Anemia Complementation Group A Intervention: Biological: RP-L102 Sponsor: Rocket Pharmaceuticals Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 30, 2020 Category: Research Source Type: clinical trials