Pilot Study of Metformin for Patients With Fanconi Anemia
Condition:   Fanconi Anemia Intervention:   Drug: metformin HCl Sponsor:   Boston Children’s Hospital Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 15, 2018 Category: Research Source Type: clinical trials

FANC-A Gene Transfer for Fanconi Anemia Using a Self-inactivating Lentiviral Vector
Condition:   Fanconi Anemia Intervention:   Genetic: Gene-modified autologous stem cells Sponsor:   Shenzhen Geno-Immune Medical Institute Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 24, 2017 Category: Research Source Type: clinical trials