Pilot Study of Metformin for Patients With Fanconi Anemia
Condition: Fanconi Anemia Intervention: Drug: metformin HCl Sponsor: Boston Children’s Hospital Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 15, 2018 Category: Research Source Type: clinical trials
FANC-A Gene Transfer for Fanconi Anemia Using a Self-inactivating Lentiviral Vector
Condition: Fanconi Anemia Intervention: Genetic: Gene-modified autologous stem cells Sponsor: Shenzhen Geno-Immune Medical Institute Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 24, 2017 Category: Research Source Type: clinical trials