A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
Condition: Fanconi Anemia Complementation Group A Intervention: Biological: RP-L102 Sponsor: Rocket Pharmaceuticals Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 24, 2019 Category: Research Source Type: clinical trials
Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Conditions: Hematologic Malignancies; Nonmalignant Diseases; Immunodeficiencies; Hemoglobinopathies; Genetic Inborn Errors of Metabolism; Fanconi's Anemia; Thalassemia; Sickle Cell Disease Intervention: Sponsor: University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials
Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients
Conditions: Hematologic Malignancies; Nonmalignant Diseases; Immunodeficiencies; Hemoglobinopathies; Genetic Inborn Errors of Metabolism; Fanconi's Anemia; Thalassemia; Sickle Cell Disease Intervention: Sponsor: University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials
Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Conditions: Hematologic Malignancies; Nonmalignant Diseases; Immunodeficiencies; Hemoglobinopathies; Genetic Inborn Errors of Metabolism; Fanconi's Anemia; Thalassemia; Sickle Cell Disease Intervention: Sponsor: University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials
Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients
Conditions: Hematologic Malignancies; Nonmalignant Diseases; Immunodeficiencies; Hemoglobinopathies; Genetic Inborn Errors of Metabolism; Fanconi's Anemia; Thalassemia; Sickle Cell Disease Intervention: Sponsor: University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials
Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Conditions: Hematologic Malignancies; Nonmalignant Diseases; Immunodeficiencies; Hemoglobinopathies; Genetic Inborn Errors of Metabolism; Fanconi's Anemia; Thalassemia; Sickle Cell Disease Intervention: Sponsor: University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials