A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
Condition:   Fanconi Anemia Complementation Group A Intervention:   Biological: RP-L102 Sponsor:   Rocket Pharmaceuticals Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 24, 2019 Category: Research Source Type: clinical trials

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Conditions:   Hematologic Malignancies;   Nonmalignant Diseases;   Immunodeficiencies;   Hemoglobinopathies;   Genetic Inborn Errors of Metabolism;   Fanconi's Anemia;   Thalassemia;   Sickle Cell Disease Intervention:   Sponsor:   University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials

Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients
Conditions:   Hematologic Malignancies;   Nonmalignant Diseases;   Immunodeficiencies;   Hemoglobinopathies;   Genetic Inborn Errors of Metabolism;   Fanconi's Anemia;   Thalassemia;   Sickle Cell Disease Intervention:   Sponsor:   University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Conditions:   Hematologic Malignancies;   Nonmalignant Diseases;   Immunodeficiencies;   Hemoglobinopathies;   Genetic Inborn Errors of Metabolism;   Fanconi's Anemia;   Thalassemia;   Sickle Cell Disease Intervention:   Sponsor:   University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials

Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients
Conditions:   Hematologic Malignancies;   Nonmalignant Diseases;   Immunodeficiencies;   Hemoglobinopathies;   Genetic Inborn Errors of Metabolism;   Fanconi's Anemia;   Thalassemia;   Sickle Cell Disease Intervention:   Sponsor:   University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Conditions:   Hematologic Malignancies;   Nonmalignant Diseases;   Immunodeficiencies;   Hemoglobinopathies;   Genetic Inborn Errors of Metabolism;   Fanconi's Anemia;   Thalassemia;   Sickle Cell Disease Intervention:   Sponsor:   University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2018 Category: Research Source Type: clinical trials