Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
Conditions: Fanconi Anemia Complementation Group A; Fanconi Anemia Intervention: Other: Safety and efficacy assessments Sponsor: Rocket Pharmaceuticals Inc. Enrolling by invitation
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials