Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

Conditions:   Fanconi Anemia Complementation Group A;   Fanconi Anemia Intervention:   Other: Safety and efficacy assessments Sponsor:   Rocket Pharmaceuticals Inc. Enrolling by invitation
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials