NHS to use world's most expensive drug to treat spinal muscular atrophy

Zolgensma, which costs £1.79m for one-off treatment, will be available in England this year for the first timeThe world ’s most expensive drug, which treats babies and young children with a rare and often fatal degenerative disorder, will be available this year for the first time on the NHS in England.Zolgensma, which costs £1.79m per dose, halts the progression ofspinal muscular atrophy (SMA), which involves loss of movement, muscle weakness and paralysis, and is the leading genetic cause of death in infants.Continue reading...
Source: Guardian Unlimited Science - Category: Science Authors: Tags: NHS Drugs Medical research Health Children Pharmaceuticals industry Society UK news England Source Type: news