An existing drug may have therapeutic potential in mitochondrial disease

(Children's Hospital of Philadelphia) New preclinical findings from extensive cell and animal studies suggest that a drug already used for a rare kidney disease could benefit patients with some mitochondrial disorders -- complex conditions with severe energy deficiency for which no proven effective treatments exist. Future clinical research is needed to explore whether the drug, cysteamine bitartrate, will meaningfully benefit patients.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news