Gene therapies for hemophilia hit the mark in clinical trials

Nature Medicine 24, 121 (2018).
doi:10.1038/nm.4492

Authors: Adrian K Pickar & Charles A Gersbach
Two recent studies describe clinical successes for single-dose gene therapy in trials for two forms of hemophilia.

Source: Nature Medicine - February 7, 2018 Category: General Medicine Authors: Adrian K Pickar Charles A Gersbach Tags: News and Views Source Type: research