Experimental Gene Therapy for Giant Axonal Neuropathy Shows Promise in NIH Clinical Trial

March 20, 2024 -- An investigational gene therapy for a rare neurodegenerative disease that begins in early childhood, known as giant axonal neuropathy (GAN), was well tolerated and showed signs of therapeutic benefit in a clinical...
Source: Drugs.com - Clinical Trials - Category: Pharmaceuticals Source Type: clinical trials