Removal of the GAA repeat in the heart of a Friedreich’s ataxia mouse model using CjCas9

Gene Therapy, Published online: 14 February 2023; doi:10.1038/s41434-023-00387-0Removal of the GAA repeat in the heart of a Friedreich’s ataxia mouse model using CjCas9

Source: Gene Therapy - February 14, 2023 Category: Genetics & Stem Cells Authors: Pouir é Yaméogo Catherine G érard Nathalie Majeau Jacques P. Tremblay Source Type: research