Spinal Muscular Atrophy Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.
High-intensity Interval Training in Patients With Spinal Muscular Atrophy
Conditions: Spinal Muscular Atrophy Interventions: Behavioral: Exercise Sponsors: Rigshospitalet, Denmark Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 16, 2024 Category: Research Source Type: clinical trials
A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal Muscular Atrophy) Patients
Conditions: SMA Interventions: Procedure: Robotically Assisted Locomotion; Procedure: Robotically Assisted Verticalization Sponsors: Wiktor Dega University Orthopedic and Rehabilitation Hospital Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 21, 2024 Category: Research Source Type: clinical trials
Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
Conditions: Spinal Muscular Atrophy Interventions: Other: evaluation of muscle function; Other: First-line cognitive assessment; Other: second-line cognitive assessment; Other: Cardiac evaluation; Radiation: MRI; Other: Assessment of activity and muscle fatigue; Other: Assessment of bulbar function; Other: Evaluation of body composition and metabolism; Other: Questionnaires; Biological: Biocollection; Other: Skinfold measurement Sponsors: Hospices Civils de Lyon Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 20, 2024 Category: Research Source Type: clinical trials
Spinal Muscular Atrophy Neonatal Screening Program
Conditions: Spinal Muscular Atrophy Interventions: Diagnostic Test: Screening SMA test Sponsors: IRCCS Burlo Garofolo Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 15, 2024 Category: Research Source Type: clinical trials
Spinal Cord Stimulation for the Treatment of Motor Deficits in People With Spinal Muscular Atrophy - Upper Limb
Conditions: Spinal Muscular Atrophy; Spinal Muscular Atrophy Type 3; Spinal Muscular Atrophy Type II; Spinal Muscular Atrophy 4; SMA Interventions: Device: Spinal Cord Stimulator (Octopolar Medtronic Vectris Leads) Sponsors: Marco Capogrosso; Roche-Genentech Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 8, 2024 Category: Research Source Type: clinical trials
An Open Label Study of Gene Therapy Product in Spinal Muscular Atrophy Patients
Conditions: Spinal Muscular Atrophy Interventions: Drug: vesemnogene lantuparvovec Sponsors: Lantu Biopharma Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 1, 2024 Category: Research Source Type: clinical trials
Assessing the Fertility Status of Men With Spinal Muscular Atrophy (SMA)
Conditions: Fertility Issues Sponsors: Bar-Chama, Natan, M.D. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 8, 2024 Category: Research Source Type: clinical trials
A Clinical Study Evaluating the Safety and Efficacy of SKG0201 Injection in Patients With Spinal Muscular Atrophy Type 1
Conditions: Spinal Muscular Atrophy 1 Interventions: Genetic: SKG0201 Injection Sponsors: Kun Sun Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 4, 2024 Category: Research Source Type: clinical trials
Real-World Use of Novel Treatments in Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Chart Review of Pediatric SMA Patients Outside of the United States
Conditions: Spinal Muscular Atrophy Sponsors: Novartis Pharmaceuticals Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 21, 2023 Category: Research Source Type: clinical trials
Two Different Treatment Modalities in Patients With Spinal Muscular Atrophy
Conditions: Muscular Atrophy, Spinal Interventions: Other: Pulmonary Rehabilitation; Other: Trunk Control Training Sponsors: Istanbul Medipol University Hospital Active, not recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 21, 2023 Category: Research Source Type: clinical trials
Safety and Usability of a Robotic Gait Device for Children and Adolescents With Neurological or Neuromuscular Disease in Their Natural Environment
Conditions: Cerebral Palsy; Acquired Brain Injury; Spinal Muscular Atrophy Interventions: Device: EXPLORER Sponsors: MarsiBionics; Hospital Infantil Universitario Ni ño Jesús, Madrid, Spain; Hospital Universitario La Paz; Hospital Universitario 12 de Octubre; Hospital General Universitario Gregorio Marañon Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 13, 2023 Category: Research Source Type: clinical trials
Test of Aquatic Mobility of SMA Infants
Conditions: Infantile Spinal Muscular Atrophy Interventions: Other: Mobility study in dry conditions; Other: Mobility study in water conditions Sponsors: Assistance Publique - H ôpitaux de Paris Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 30, 2023 Category: Research Source Type: clinical trials
Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Conditions: Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including; Sickle Cell Disease; Cystic Fibrosis; Fragile X Syndrome; Proximal Spinal Muscular Atrophy; Myotonic Dystrophy; Muscular Dystrophy, Duchenne; Muscular Dystrophy, Becker; Neurofibromatosis-Noonan Syndrome; Huntington Disease; Hemophilia A; Hemophilia B; MODY2 Diabetes; X-Linked Hydrocephalus; Autosomal Recessive Polycystic Kidney Disease Interventions: Biological: Blood sample Sponsors: Assistance Publique - H ôpitaux de Paris Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 27, 2023 Category: Research Source Type: clinical trials
Spinal Cord Gray Matter Imaging in Spinal Muscular Atrophy
Conditions: Spinal Muscular Atrophy Type III; Spinal Muscular Atrophy Type II Interventions: Diagnostic Test: MRI Sponsors: University Hospital, Basel, Switzerland Enrolling by invitation (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 17, 2023 Category: Research Source Type: clinical trials
NMD Pharma initiates Phase II trial of NMD670 in Spinal Muscular Atrophy
Aarhus, Denmark, 26 September 2023– NMD Pharma A/S, a clinical-stage biotech company developing first-in-class, small molecule ClC-1 inhibitors directly targeting muscle function within neuromuscular disorders, today announces that the first... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - September 26, 2023 Category: Pharmaceuticals Source Type: clinical trials