Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients
Condition:   SMA II Intervention:   Genetic: GC101 Sponsor:   GeneCradle Inc Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 13, 2023 Category: Research Source Type: clinical trials

The Effect of Spinal Orthosis on the Development of Scoliosis and Chest Deformity in Type I Spinal Muscular Atrophy
Conditions:   Spinal Muscular Atrophy Type I;   Scoliosis;   Chest Deformities;   Spinal Orthosis;   Pulmonary Rehabilitation Interventions:   Device: Thoracolumbosacral Spinal Orthosis (TLSO);   Other: Pulmonary Rehabilitation(PR) and Pulmonary Care (PC) Sponsor:   Medipol University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 26, 2023 Category: Research Source Type: clinical trials