Spinal Muscular Atrophy Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition: Muscular Atrophy, Spinal Intervention: Drug: risdiplam Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Condition: Spinal Muscular Atrophy Intervention: Genetic: GC101 Sponsor: GeneCradle Inc Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 21, 2023 Category: Research Source Type: clinical trials