A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Condition:   Muscular Atrophy, Spinal Intervention:   Drug: risdiplam Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 17, 2023 Category: Research Source Type: clinical trials

Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Condition:   Spinal Muscular Atrophy Intervention:   Genetic: GC101 Sponsor:   GeneCradle Inc Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 21, 2023 Category: Research Source Type: clinical trials