Acadia Pharmaceuticals Announces Positive Top-line Results from the Pivotal Phase 3 Lavender Trial of Trofinetide in Rett Syndrome
Trofinetide met co-primary efficacy endpoints demonstrating statistically significant improvement over placebo in the Rett Syndrome Behaviour Questionnaire (RSBQ) (p=0.0175) and the Clinical Global Impression of Improvement (CGI-I)... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - December 6, 2021 Category: Pharmaceuticals Source Type: clinical trials

Measuring Impact of Computer Gaming on Arm Use in Rett Syndrome
Condition:   Rett Syndrome Intervention:   Behavioral: Modified Virtual Reality Gaming Sponsors:   Georgetown University;   International Rett Syndrome Foundation Rettsyndrome.org Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 19, 2021 Category: Research Source Type: clinical trials