A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children With Rett Syndrome
Condition: Rett Syndrome Intervention: Genetic: NGN-401 Sponsor: Neurogene Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 12, 2023 Category: Research Source Type: clinical trials
A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children With Rett Syndrome
Condition: Rett Syndrome Intervention: Genetic: NGN-401 Sponsor: Neurogene Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 12, 2023 Category: Research Source Type: clinical trials
A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children With Rett Syndrome
Condition: Rett Syndrome Intervention: Genetic: NGN-401 Sponsor: Neurogene Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 12, 2023 Category: Research Source Type: clinical trials
Gene Editing as a Therapeutic Approach for Rett Syndrome
Condition: Rett Syndrome Intervention: Other: Gene editing in vitro Sponsor: University of Siena Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 23, 2023 Category: Research Source Type: clinical trials