A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children With Rett Syndrome
Condition:   Rett Syndrome Intervention:   Genetic: NGN-401 Sponsor:   Neurogene Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 12, 2023 Category: Research Source Type: clinical trials

A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children With Rett Syndrome
Condition:   Rett Syndrome Intervention:   Genetic: NGN-401 Sponsor:   Neurogene Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 12, 2023 Category: Research Source Type: clinical trials

A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children With Rett Syndrome
Condition:   Rett Syndrome Intervention:   Genetic: NGN-401 Sponsor:   Neurogene Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 12, 2023 Category: Research Source Type: clinical trials

Gene Editing as a Therapeutic Approach for Rett Syndrome
Condition:   Rett Syndrome Intervention:   Other: Gene editing in vitro Sponsor:   University of Siena Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 23, 2023 Category: Research Source Type: clinical trials