An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome
Condition: Rett Syndrome Intervention: Drug: Trofinetide Sponsor: ACADIA Pharmaceuticals Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 4, 2021 Category: Research Source Type: clinical trials
Development of the ORCA Communication Measure for Rett Syndrome
Condition: Rett Syndrome Intervention: Sponsors: Rett Syndrome Research Trust; Duke University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 9, 2021 Category: Research Source Type: clinical trials