An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome
Condition:   Rett Syndrome Intervention:   Drug: Trofinetide Sponsor:   ACADIA Pharmaceuticals Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 4, 2021 Category: Research Source Type: clinical trials

Development of the ORCA Communication Measure for Rett Syndrome
Condition:   Rett Syndrome Intervention:   Sponsors:   Rett Syndrome Research Trust;   Duke University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 9, 2021 Category: Research Source Type: clinical trials