A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Conditions: Duchenne Muscular Dystrophy Interventions: Genetic: SGT-003 Sponsors: Solid Biosciences Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 18, 2023 Category: Research Source Type: clinical trials

Study of ARO-DM1 in Subjects With Type 1 Myotonic Dystrophy
Conditions: Myotonic Dystrophy 1 Interventions: Drug: ARO-DM1 for Injection; Drug: Placebo Sponsors: Arrowhead Pharmaceuticals Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 18, 2023 Category: Research Source Type: clinical trials

Superior Cervical Sympathetic Block Versus Stellate Ganglion Block in Post-traumatic Subarachnoid Hemorrhage
Conditions: Post-Traumatic Subarachnoid Hemorrhage Interventions: Procedure: Superior cervical sympathetic block group; Procedure: Stellate ganglion block group Sponsors: Assiut University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 16, 2023 Category: Research Source Type: clinical trials

A 5-year Natural History Study in LAMA2-related Muscular Dystrophy and SELENON-related Myopathy.
Conditions: LAMA2-related Muscular Dystrophy; SELENON-related Myopathy Interventions: Other: No intervention Sponsors: Radboud University Medical Center Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 15, 2023 Category: Research Source Type: clinical trials

Study of ARO-DUX4 in Adult Patients With Facioscapulohumeral Muscular Dystrophy Type 1
Conditions: Facio-Scapulo-Humeral Dystrophy Interventions: Drug: ARO-DUX4 for Injection; Drug: Placebo Sponsors: Arrowhead Pharmaceuticals Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 15, 2023 Category: Research Source Type: clinical trials

The Comparison of Sympathetic Blockade of Stellate Ganglion Block and Thoracic Sympathetic Ganglion Block
Conditions: Chronic Pain; Neuropathic Pain; Complex Regional Pain Syndromes; Post Herpetic Neuralgia; Post Laminectomy Syndrome Interventions: Procedure: Stellate Ganglion Block (SGB); Procedure: Thoracic Sympathetic Ganglion Block (TSGB) Sponsors: Seoul National University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 14, 2023 Category: Research Source Type: clinical trials

Vestibulo-Ocular Reflex Function in Individuals With Chronic Motion Sensitivity Cross-Sectional Study
Conditions: Motion Sickness Sponsors: Loma Linda University Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 13, 2023 Category: Research Source Type: clinical trials

A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)
Conditions: Duchenne Muscular Dystrophy Interventions: Genetic: delandistrogene moxeparvovec Sponsors: Hoffmann-La Roche; Sarepta Therapeutics, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 13, 2023 Category: Research Source Type: clinical trials

Remote Study: Wearable Technology to Evaluate Hyperglycemia and HRV in DMD
Conditions: Duchenne Muscular Dystrophy Interventions: Device: wearable technology Sponsors: Vanderbilt University Medical Center Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 9, 2023 Category: Research Source Type: clinical trials

A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)
Conditions: Duchenne Muscular Dystrophy Interventions: Biological: JWK007 Single intravenous infusion administration Sponsors: West China Hospital Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 2, 2023 Category: Research Source Type: clinical trials

Thoracoscopic Sympathetic Chain Interruption for Palmar Hyperhidrosis in Patients Below 18
Conditions: Hyperhidrosis; Children, Adolescents; Thoracoscopic Sympathetic Chain Interruption; Sympathetic Disorder Interventions: Procedure: Thoracoscopic sympathectomy; Procedure: Thoracoscopic sympathotomy; Procedure: Thoracoscopic sympathetic chain clipping Sponsors: dr. Muhammad Abdelhafez Mahmoud, MD Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 2, 2023 Category: Research Source Type: clinical trials

Thermovision-controlled Lumbar Sympathetic Blockade in Chronic Limb-threatening Ischemia Treatment
Conditions: Chronic Limb-Threatening Ischemia Interventions: Procedure: lumbar sympathetic blockade Sponsors: Europainclinics z. ú.; Slovak Academy of Sciences Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 1, 2023 Category: Research Source Type: clinical trials

Telerehabilitation-based Motor Imagery Training in Children With Duchenne Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy Interventions: Procedure: telerehabilitation-based motor imagery training; Procedure: telerehabilitation-based physiotheraphy training Sponsors: Hacettepe University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 31, 2023 Category: Research Source Type: clinical trials

Remote Physiotherapy to Protect Physcial Health in Duchenne Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy Interventions: Other: Telerehabilitation Sponsors: Lokman Hekim Üniversitesi Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 26, 2023 Category: Research Source Type: clinical trials

A Multicenter Phenotype-Genotype Analysis of DM1 Patients in China
Conditions: Myotonic Dystrophy 1 Interventions: Diagnostic Test: Brain MRI scan Sponsors: Huashan Hospital Enrolling by invitation (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 26, 2023 Category: Research Source Type: clinical trials