Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy
Conditions: DMD-Associated Dilated Cardiomyopathy Interventions: Genetic: SRD-001 Sponsors: Sardocor Corp. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 25, 2024 Category: Research Source Type: clinical trials

Over-the-Counter Antihistamines & Heat Stress
Conditions: Heat Illness; Allergic Rhinitis; Heat Injury; Sudomotor Sympathetic Dysfunction Interventions: Drug: 50 mg Diphenhydramine; Drug: 10 mg Loratadine; Drug: 5 mg Desloratadine; Other: Placebo (Sugar Pill) Sponsors: Lakehead University Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 22, 2024 Category: Research Source Type: clinical trials

Effect of Combined Lumbar Traction and Repetitive Back Extension Exercise on H-reflex in Lumbosacral Radiculopathy
Conditions: Lumbosacral Radiculopathy; McKenzie Derangement Syndrome Interventions: Other: Repeated back extension exercise (McKenzie); Device: Mechanical traction Sponsors: Cairo University Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 22, 2024 Category: Research Source Type: clinical trials

Fellow-eye Study (FE) of LX101 in Subjects With Inherited Retinal Dystrophy
Conditions: Inherited Retinal Dystrophy Interventions: Genetic: LX101 Sponsors: Innostellar Biotherapeutics Co.,Ltd Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 18, 2024 Category: Research Source Type: clinical trials

Contralateral R1 in Amyotrophic Lateral Sclerosis
Conditions: Amyotrophic Lateral Sclerosis Interventions: Diagnostic Test: blink reflex evaluation Sponsors: Hospices Civils de Lyon Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 15, 2024 Category: Research Source Type: clinical trials

Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1
Conditions: Myotonic Dystrophy 1 Interventions: Drug: PGN-EDODM1; Other: Placebo Sponsors: PepGen Inc Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 12, 2024 Category: Research Source Type: clinical trials

Neodymium-doped Yttrium Aluminum Garnet (Nd:YAG) Laser Treatment for Granular Corneal Dystrophy
Conditions: Granular Dystrophy, Corneal Interventions: Device: Nd:YAG Laser Sponsors: Johns Hopkins University Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 11, 2024 Category: Research Source Type: clinical trials

Safety and Tolerability of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations
Conditions: Inherited Retinal Dystrophy Associated With RPE65 Mutations Interventions: Genetic: LX101 Sponsors: Innostellar Biotherapeutics Co.,Ltd Active, not recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 9, 2024 Category: Research Source Type: clinical trials

Effectiveness of Aquatic Therapy in Children With Duchenne and Becker Muscular Dystrophy
Conditions: Duchenne or Becker Muscular Dystrophy Interventions: Other: Aquatic Therapy Group; Other: Conventional Physical Therapy Group Sponsors: Gaziosmanpasa Research and Education Hospital Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 1, 2024 Category: Research Source Type: clinical trials

A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia
Conditions: Oculopharyngeal Muscular Dystrophy Interventions: Genetic: BB-301: Dose escalation phase 1b cohort 1; Genetic: BB-301: Dose escalation phase 1b cohort 2; Genetic: BB-301: Dose escalation phase 1b cohort 3; Genetic: BB-301: Dose expansion phase 2a Sponsors: Benitec Biopharma, Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 29, 2023 Category: Research Source Type: clinical trials

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)
Conditions: Myotonic Dystrophy Type 1 (DM1) Interventions: Drug: VX-670; Drug: Placebo Sponsors: Vertex Pharmaceuticals Incorporated Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 29, 2023 Category: Research Source Type: clinical trials

Validity and Reliability of the 6 Minute Pegboard Ring Test
Conditions: Duchenne Muscular Dystrophy Sponsors: Çağtay Maden Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 18, 2023 Category: Research Source Type: clinical trials

Early Feasibility Study of the MyoRegulator ® for Treatment of ALS
Conditions: Amyotrophic Lateral Sclerosis Interventions: Device: MyoRegulator ® Sponsors: PathMaker Neurosystems Inc.; Spaulding Rehabilitation Hospital; Sean M. Healey& AMG Center for ALS; Muscular Dystrophy Association Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 11, 2023 Category: Research Source Type: clinical trials

National Registry of Cardioneuroablation in Recurrent Reflex Syncope
Conditions: Syncope, Vasovagal; Bradycardia; Heart Arrest Interventions: Procedure: Cardioneuroablation Sponsors: University Hospital, Bordeaux Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 7, 2023 Category: Research Source Type: clinical trials

Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Conditions: Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including; Sickle Cell Disease; Cystic Fibrosis; Fragile X Syndrome; Proximal Spinal Muscular Atrophy; Myotonic Dystrophy; Muscular Dystrophy, Duchenne; Muscular Dystrophy, Becker; Neurofibromatosis-Noonan Syndrome; Huntington Disease; Hemophilia A; Hemophilia B; MODY2 Diabetes; X-Linked Hydrocephalus; Autosomal Recessive Polycystic Kidney Disease Interventions: Biological: Blood sample Sponsors: Assistance Publique - H ôpitaux de Paris Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 27, 2023 Category: Research Source Type: clinical trials