Scientists Discover Potential Treatment Approaches for Polycystic Kidney Disease
April 4, 2024 -- Researchers have shown that dangerous cysts, which form over time in polycystic kidney disease (PKD), can be prevented by a single normal copy of a defective gene. This means the potential exists that scientists could one day tailor... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - April 4, 2024 Category: Pharmaceuticals Source Type: clinical trials

A Phase 1 Study to Evaluate Safety, Tolerability, and Pharmacokinetics (PK) of VX-407 in Healthy Participants
Conditions: Autosomal Dominant Polycystic Kidney Disease (ADPKD) Interventions: Drug: VX-407; Drug: Placebo; Drug: Midazolam Sponsors: Vertex Pharmaceuticals Incorporated Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 3, 2024 Category: Research Source Type: clinical trials

Well-Formulated Ketogenic Diet Polycystic Kidney Disease
Conditions: Polycystic Kidney Disease Interventions: Other: Ketogenic Diet; Biological: Ketone/Glucose Monitoring; Biological: CGM/CKM; Biological: Blood Draw; Other: Body Composition; Other: Change in glomerular filtration rate (mg/mmol) via magnetic resonance imaging (MRI) . Sponsors: Ohio State University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 22, 2024 Category: Research Source Type: clinical trials

Study of Tamibarotene in Patients With ADPKD
Conditions: Autosomal Dominant Polycystic Kidney Disease (ADPKD) Interventions: Drug: Tamibarotene; Drug: Placebo Sponsors: Rege Nephro Co., Ltd. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 4, 2024 Category: Research Source Type: clinical trials

Safety of RotigotiNe in Patients With Autosomal Dominant Polycystic Kidney Disease
Conditions: Kidney Diseases Interventions: Drug: standard care + rotigotine at 4 mg/24h for 24 months.; Drug: standard care for 24 months. Sponsors: University Hospital, Rouen Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 4, 2024 Category: Research Source Type: clinical trials

HYDROchlorothiazide versus placebo to PROTECT polycystic kidney disease patients and improve their quality of life: study protocol and rationale for the HYDRO-PROTECT randomized controlled trial
ConclusionThe HYDRO-PROTECT study will demonstrate whether co-treatment with HCT can improve the renoprotective efficacy and tolerability of tolvaptan in patients with ADPKD. (Source: Trials)
Source: Trials - February 14, 2024 Category: Research Source Type: clinical trials

Outcome of ADPKD With Octreotide LAR
Conditions: Autosomal Dominant Polycystic Kidney Interventions: Drug: Octreotide Sponsors: Mario Negri Institute for Pharmacological Research Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 5, 2024 Category: Research Source Type: clinical trials

Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Conditions: Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including; Sickle Cell Disease; Cystic Fibrosis; Fragile X Syndrome; Proximal Spinal Muscular Atrophy; Myotonic Dystrophy; Muscular Dystrophy, Duchenne; Muscular Dystrophy, Becker; Neurofibromatosis-Noonan Syndrome; Huntington Disease; Hemophilia A; Hemophilia B; MODY2 Diabetes; X-Linked Hydrocephalus; Autosomal Recessive Polycystic Kidney Disease Interventions: Biological: Blood sample Sponsors: Assistance Publique - H ôpitaux de Paris Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 27, 2023 Category: Research Source Type: clinical trials

Treat Autosomal Dominant Polycystic Kidney Disease With Oral Ketone Ester?
Conditions: ADPKD Interventions: Dietary Supplement: Ketone ester Sponsors: Universitair Ziekenhuis Brussel Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 25, 2023 Category: Research Source Type: clinical trials

Genetic Testing in Autosomal Dominant Polycystic Kidney Disease
Conditions: ADPKD Interventions: Other: Survey Sponsors: University of California, San Francisco Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 17, 2023 Category: Research Source Type: clinical trials

National Registry of Rare Kidney Diseases
Conditions: Adenine Phosphoribosyltransferase Deficiency; AH Amyloidosis; AHL Amyloidosis; AL Amyloidosis; Alport Syndrome; Atypical Hemolytic Uremic Syndrome; Autoimmune Distal Renal Tubular Acidosis; Autosomal Recessive Proximal Renal Tubular Acidosis; Autosomal Recessive Distal Renal Tubular Acidosis; Autosomal Dominant Polycystic Kidney Disease; Autosomal Recessive Polycystic Kidney Disease; Bartter Syndrome; BK Nephropathy; C3 Glomerulopathy With Monoclonal Gammopathy; C3 Glomerulopathy; Calciphylaxis; Crystalglobulinaemia; Crystal-storing Histiocytosis; Cystinosis; Cystinuria; Dense Deposit Disease; Dent Disease; Den...
Source: ClinicalTrials.gov - October 4, 2023 Category: Research Source Type: clinical trials

Study and Management of Cystic Complications in Autosomal Dominant Polycystic Kidney Disease
Condition:   Polycystic Kidney Diseases Intervention:   Sponsor:   University Hospital, Brest Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 14, 2023 Category: Research Source Type: clinical trials