BH4 Responsiveness in PAH Deficiency PKU Patients
Conditions: Pku Phenylketonuria; PAH Deficiency Intervention: Drug: BH4 Sponsors: Taipei Veterans General Hospital, Taiwan; BioMarin Pharmaceutical Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 13, 2020 Category: Research Source Type: clinical trials
Short-term Effects of Good Metabolic Control on Cognitive Function, Wellbeing, and Metabolic Parameters in Adult Patients With Phenylketonuria
Condition: Phenylketonurias Intervention: Other: PHE-diet Sponsor: Klaus Parhofer Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 24, 2019 Category: Research Source Type: clinical trials