BH4 Responsiveness in PAH Deficiency PKU Patients
Conditions:   Pku Phenylketonuria;   PAH Deficiency Intervention:   Drug: BH4 Sponsors:   Taipei Veterans General Hospital, Taiwan;   BioMarin Pharmaceutical Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 13, 2020 Category: Research Source Type: clinical trials

Short-term Effects of Good Metabolic Control on Cognitive Function, Wellbeing, and Metabolic Parameters in Adult Patients With Phenylketonuria
Condition:   Phenylketonurias Intervention:   Other: PHE-diet Sponsor:   Klaus Parhofer Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 24, 2019 Category: Research Source Type: clinical trials