Evaluation of Capillary Blood Collection Devices (Mitra ® and HemaPEN®)
Conditions: Phenylketonuria; Metabolic Diseases Intervention: Diagnostic Test: DM-DIV MITRA® Sponsor: University Hospital, Grenoble Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 8, 2023 Category: Research Source Type: clinical trials
PTC Therapeutics Announces APHENITY Trial Achieved Primary Endpoint with Sepiapterin in PKU Patients
SOUTH PLAINFIELD, N.J., May 17, 2023. PTC Therapeutics, Inc. today announced that the primary endpoint was achieved in the APHENITY, Phase 3 registration-directed clinical trial of sepiapterin in adult and pediatric patients with phenylketonuria... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - May 17, 2023 Category: Pharmaceuticals Source Type: clinical trials
Synlogic Receives Orphan Drug Designation from FDA for SYNB1934 for Treatment of Phenylketonuria
CAMBRIDGE, Mass., May 09, 2023 (GLOBE NEWSWIRE) -- Synlogic, Inc. (Nasdaq: SYBX), the leading company advancing therapeutics based on synthetic biology, today announced that the U.S. Food and Drug Administration (FDA) has granted orphan drug... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - May 9, 2023 Category: Pharmaceuticals Source Type: clinical trials
First-in-Human, Multiple Part Clinical Study of JNT-517 in Healthy Participants and in Participants With Phenylketonuria
Condition: Phenylketonuria Interventions: Drug: JNT-517 Suspension; Drug: Placebo Suspension; Drug: JNT-517 Tablet; Drug: Placebo Tablet Sponsor: Jnana Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 23, 2023 Category: Research Source Type: clinical trials
