Nutritional Impacts of Palynziq on Patients With Phenylketonuria (PKU)
Condition: Phenylketonurias Intervention: Drug: Palynziq Sponsors: Emory University; BioMarin Pharmaceutical Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 27, 2020 Category: Research Source Type: clinical trials
Acceptability and Tolerance of a Ready-to-use Protein Substitute in Tablet Form for the Dietary Management of Phenylketonuria
Conditions: Phenylketonurias; Hyperphenylalaninaemia; Tetrahydrobiopterin Deficiency Intervention: Dietary Supplement: Phenylalanine-free protein substitute in tablet form (XPhe minis) Sponsors: metaX Institut fuer Diatetik GmbH; Birmingham Children’s Hospital Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 5, 2020 Category: Research Source Type: clinical trials