A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
Conditions: Progressive Familial Intrahepatic Cholestasis; Alagille Syndrome; Cholestatic Liver Disease Intervention: Drug: Maralixibat Sponsor: Mirum Pharmaceuticals, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 28, 2021 Category: Research Source Type: clinical trials