A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
Conditions:   Progressive Familial Intrahepatic Cholestasis;   Alagille Syndrome;   Cholestatic Liver Disease Intervention:   Drug: Maralixibat Sponsor:   Mirum Pharmaceuticals, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 28, 2021 Category: Research Source Type: clinical trials