The Natural History of Acquired and Inherited Bone Marrow Failure Syndromes.
Conditions:   Severe Aplastic Anemia;   Telomere Biology Disorders;   Inherited Bone Marrow Failure Syndromes Intervention:   Sponsor:   National Heart, Lung, and Blood Institute (NHLBI) Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 19, 2021 Category: Research Source Type: clinical trials

Reduced Intensity BMT for Immune Dysregulatory and Bone Marrow Failure Syndromes Using Post-Transplant Cyclophosphamide
Conditions:   Primary Immune Deficiency Disorder;   Immune Deficiency Disease;   Bone Marrow Failure Interventions:   Drug: Alemtuzumab;   Drug: Fludarabine;   Drug: Melphalan;   Radiation: Low Dose Total Body Irradiation;   Drug: Cyclophosphamide;   Drug: Tacrolimus;   Drug: Mycophenolate Mofetil Sponsor:   Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 18, 2020 Category: Research Source Type: clinical trials

Reduced Intensity BMT for Immune Dysregulatory and Bone Marrow Failure Syndromes Using Post-Transplant Cyclophosphamide
Conditions:   Primary Immune Deficiency Disorder;   Immune Deficiency Disease;   Bone Marrow Failure Interventions:   Drug: Alemtuzumab;   Drug: Fludarabine;   Drug: Melphalan;   Radiation: Low Dose Total Body Irradiation;   Drug: Cyclophosphamide;   Drug: Tacrolimus;   Drug: Mycophenolate Mofetil Sponsor:   Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 18, 2020 Category: Research Source Type: clinical trials

A Clinical Trial of CK0801 (a New Drug) in Patients With Bone Marrow Failure Syndrome (BMF)
Condition:   Bone Marrow Disease Intervention:   Biological: CK0801 Sponsor:   Cellenkos, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 12, 2018 Category: Research Source Type: clinical trials