Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice
Gene Therapy, Published online: 08 February 2021; doi:10.1038/s41434-021-00224-2Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Sam Hana Michael Peterson Helen McLaughlin Eric Marshall Attila J. Fabian Olivia McKissick Kathryn Koszka Galina Marsh Michael Craft Shanqin Xu Alexander Sorets Tess Torregrosa Chao Sun Chris E. Henderson Shih-Ching Lo Source Type: research