New developments in gene editing for Duchenne muscular dystrophy

Nature Reviews Cardiology, Published online: 11 February 2020; doi:10.1038/s41569-020-0350-7A somatic gene editing therapy for the treatment of Duchenne muscular dystrophy (DMD) improves skeletal and cardiac muscle function and reduces cardiac arrhythmogenic vulnerability in a pig model of DMD and an in vitro model of human DMD.
Source: Nature Reviews Cardiology - Category: Cardiology Authors: Source Type: research