A Phase 2 Study to Evaluate the Safety, Tolerability, PK and PD in Cystic Fibrosis Patients With at Least 1 G542X Allele
Conditions: Genetic Disease; Nonsense Mutation; Cystic Fibrosis With Meconium Ileus Intervention: Drug: ELX-02 Sponsor: Eloxx Pharmaceuticals, Inc. Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials