Gene editing for recessive dystrophic epidermolysis bullosa

(Universidad Carlos III de Madrid) A group of researchers from the Biomedical Research Networking Centre on Rare Diseases (CIBERER), Universidad Carlos III de Madrid (UC3M), the Research Center for Energy, Environmental and Technology (CIEMAT), and the Instituto de Investigaci ó n Sanitaria Fundaci ó n Jim é nez D í az (IIS-FJD) have led a study which demonstrates the viability of a gene editing strategy for recessive dystrophic epidermolysis bullosa (also known as butterfly chilidren) with the tool CRISPR/Cas9 in preclinical models with this disease.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news