Cystic fibrosis drug combo found safe and effective for 2- to 5-year-olds

(Ann& Robert H. Lurie Children's Hospital of Chicago) An open label Phase 3 study conducted at Ann& Robert H. Lurie Children's Hospital of Chicago and other centers established that a combination of cystic fibrosis drugs lumacaftor and ivacaftor is safe and effective in children aged 2-5 years, whose disease is caused by two copies of F508del-CFTR gene mutation -- the most common and severe form of cystic fibrosis.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news