WiTNNess - TNNT1 Myopathy Natural History Study
Conditions: TNNT1-associated Myopathy; Infantile-onset Nemaline Rod Myopathy; Myopathies, Nemaline; Myopathy; Myopathy, Rod; Myopathy; Hereditary; Amish Nemaline Myopathy; Nemaline Myopathy 5; NEM5; Genetic Muscle Disease; Recessive Hereditary Disorder (Autosomal); ANM Sponsors: Clinic for Special Children Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials