First trial of gene therapy for cystic fibrosis to show beneficial effect on lung function

For the first time gene therapy for cystic fibrosis has shown a significant benefit in lung function compared with placebo, in a phase 2 randomized trial. The technique replaces the defective gene response for cystic fibrosis by using inhaled molecules of DNA to deliver a normal working copy of the gene to lung cells.

Source: ScienceDaily Headlines - July 3, 2015 Category: Science Source Type: news