FDA OKs Gene Therapy for Metachromatic Leukodystrophy FDA OKs Gene Therapy for Metachromatic Leukodystrophy

Atidarsagene autotemcel (Lenmeldy) is approved for presymptomatic late infantile, presymptomatic early juvenile, or early symptomatic early juvenile MLD.Medscape Medical News
Source: Medscape Neurology and Neurosurgery Headlines - Category: Neurology Tags: Neurology & Neurosurgery Source Type: news