Barriers to gene therapy, understanding the concerns people with haemophilia have: an exigency sub-study
Gene therapy has the potential to offer people with haemophilia (PwH) a life free from bleeding and the burden posed by current treatment regimens. To date, gene therapy has only been available in clinical tri...
Source: Orphanet Journal of Rare Diseases - Category: Internal Medicine Authors: Simon Fletcher, Kathryn Jenner, Michael Holland and Kate Khair Tags: Research Source Type: research
More News: Bleeding | Gene Therapy | Genetics | Haemophilia | Hemophilia | Internal Medicine | Rare Diseases | Study