A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4 (EMERGENE)

Conditions: Limb-girdle Muscular Dystrophy Interventions: Biological: SRP-9003; Drug: Glucocorticoid Sponsors: Sarepta Therapeutics, Inc. Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials