N-terminal titin fragment: a non-invasive, pharmacodynamic biomarker for microdystrophin efficacy
Multiple clinical trials to assess the efficacy of AAV-directed gene transfer in participants with Duchenne muscular dystrophy (DMD) are ongoing. The success of these trials currently relies on standard functi...
Source: Skeletal Muscle - Category: Research Authors: Jessica F. Boehler, Kristy J. Brown, Valeria Ricotti and Carl A. Morris Tags: Research Source Type: research
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