Treatment response and neurofilament light chain levels with long-term patisiran in hereditary transthyretin-mediated amyloidosis with polyneuropathy: 24-month results of an open-label extension study

.

Source: Amyloid: The Journal of Protein Folding Disorders - July 20, 2023 Category: Biochemistry Authors: Simina TicauEmre AldincMichael PolydefkisDavid AdamsTeresa CoelhoMitsuharu UedaCecilia HaleJohn VestPaul Nioia Alnylam Pharmaceuticals, Cambridge, MA, USAb Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD, USAc Neurology Source Type: research