Epidemiology and patient journey of Rett syndrome in the United States: a real-world evidence study

Rett syndrome (RTT) is a neurodevelopmental disorder that almost exclusively affects females and is associated with high clinical burden. However, literature characterizing the real-world journey of patients w...

Source: BMC Neurology - April 4, 2023 Category: Neurology Authors: Damian May, Kal é Kponee-Shovein, Malena Mahendran, Nathaniel Downes, Kristy Sheng, Patrick Lefebvre and Wendy Y. Cheng Tags: Research Source Type: research