FDA OKs First Drug for Rett Syndrome FDA OKs First Drug for Rett Syndrome

Trofinetide (Daybue) is for adults and children aged 2 years and older with Rett syndrome, a rare, genetic neurodevelopmental disorder affecting mostly females.Medscape Medical News
Source: Medscape Neurology and Neurosurgery Headlines - Category: Neurology Tags: Neurology & Neurosurgery News Alert Source Type: news