Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease
Gene Therapy, Published online: 11 January 2023; doi:10.1038/s41434-022-00381-yPreclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Jey M. Jeyakumar Azadeh Kia Lawrence C. S. Tam Jenny McIntosh Justyna Spiewak Kevin Mills Wendy Heywood Elisa Chisari Noemi Castaldo Dani ël Verhoef Paniz Hosseini Petya Kalcheva Clement Cocita Carlos J. Miranda Miriam Canavese Jaminder Khinder Cecilia R Source Type: research