Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease

Gene Therapy, Published online: 11 January 2023; doi:10.1038/s41434-022-00381-yPreclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Source Type: research