A novel preclinical model of mucopolysaccharidosis type II for developing human hematopoietic stem cell gene therapy

Gene Therapy, Published online: 14 July 2022; doi:10.1038/s41434-022-00357-yA novel preclinical model of mucopolysaccharidosis type II for developing human hematopoietic stem cell gene therapy

https://www.nature.com/articles/s41434-022-00357-y

Source: Gene Therapy - July 14, 2022 Category: Genetics & Stem Cells Authors: Yohta Shimada Natsumi Ishii Takashi Higuchi Motohito Goto Toya Ohashi Hiroshi Kobayashi Source Type: research

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