Courtney D. Thornburg, MD, MS  - Using Prophylactic Treatment Strategies to Improve Quality of Life and Adherence in Children With Hemophilia
Using Prophylactic Treatment Strategies to Improve Quality of Life and Adherence in Children With Hemophilia (Source: PeerView CME/CE Video Podcast - Hematology)
Source: PeerView CME/CE Video Podcast - Hematology - November 19, 2014 Category: Hematology Authors: PVI, PeerView Institute for Medical Education Tags: Science, Medicine Source Type: video

Courtney D. Thornburg, MD, MS - Using Prophylactic Treatment Strategies to Improve Quality of Life and Adherence in Children With Hemophilia
Using Prophylactic Treatment Strategies to Improve Quality of Life and Adherence in Children With Hemophilia (Source: Peerview CME/CE Video Podcast - Internal Medicine International)
Source: Peerview CME/CE Video Podcast - Internal Medicine International - November 19, 2014 Category: Internal Medicine Authors: PVI, PeerView Institute for Medical Education Tags: Science, Medicine Source Type: video

Genetic Therapies for Genetic Diseases: Results and Lessons from Recent Successes
Wednesday Afternoon Lecture Series The disease burden represented by genetic disease is high. Genetic diseases account for nearly half of all admissions to children’s hospitals, yet therapeutic options for many of these are limited. The goal of gene therapy is to harness the power of the Human Genome Project to provide better alternatives for those with genetic diseases. After two decades of clinical investigation of gene therapy, the field is able to point to several successes and one licensed product (an AAV vector for lipoprotein lipase deficiency). This lecture will review the vectors that have performed best in the...
Source: Videocast - All Events - May 28, 2013 Category: Journals (General) Tags: Upcoming Events Source Type: video