Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM)
Condition:   Myotubular MyopathyIntervention:   Sponsors:   Valerion Therapeutics, LLC;   Institut de Myologie, France;   GenethonRecruiting - verified September 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 4, 2014 Category: Research Source Type: clinical trials