The Natural History and Muscle Fatigability of Patients With Congenital Myopathies.
Conditions: Central Core Disease; Multi-Minicore Disease; Nemaline Myopathy; Centronuclear Myopathy Interventions: Other: Natural history and non therapeutical therapy Sponsors: Radboud University Medical Center; UMC Utrecht Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 5, 2023 Category: Research Source Type: clinical trials

Astellas Announces Data from ASPIRO Study for AT132 (resamirigene bilparvovec) in X-linked Myotubular Myopathy Published in The Lancet Neurology
TOKYO, Nov. 15, 2023 /PRNewswire/ -- Astellas Pharma Inc. (TSE: 4503, President and CEO: Naoki Okamura, " Astellas " ) today announced that The Lancet Neurology published a preliminary data analysis from the ASPIRO trial, evaluating... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - November 15, 2023 Category: Pharmaceuticals Source Type: clinical trials

Astellas Provides Update on ASPIRO Clinical Trial of AT132 in Patients with X-linked Myotubular Myopathy
TOKYO, September 1, 2021 /PRNewswire/ -- Astellas Pharma Inc. (TSE: 4503, President and CEO: Kenji Yasukawa, Ph.D., " Astellas " ) announced that it has voluntarily paused screening and dosing of additional participants in its... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - September 1, 2021 Category: Pharmaceuticals Source Type: clinical trials

Natural History Study of Patients With Centronuclear Myopathies
Condition:   Centronuclear Myopathy Intervention:   Sponsor:   Dynacure Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 27, 2021 Category: Research Source Type: clinical trials

Tamoxifen Therapy for Myotubular Myopathy
Condition:   X Linked Myotubular Myopathy Interventions:   Drug: ApoTamox 10mg;   Drug: Placebo Sponsors:   James Dowling;   Canadian Institutes of Health Research (CIHR);   Cures Within Reach;   The Joshua Frase Foundation USA;   Will Cure USA;   Mogford Campbell Family Chair Fund Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 7, 2021 Category: Research Source Type: clinical trials