Tamoxifen Therapy for Myotubular Myopathy
Condition:   X Linked Myotubular Myopathy Interventions:   Drug: ApoTamox 10mg;   Drug: Placebo Sponsors:   James Dowling;   Canadian Institutes of Health Research (CIHR);   Cures Within Reach;   The Joshua Frase Foundation USA;   Will Cure USA;   Mogford Campbell Family Chair Fund;   Myotubular Trust Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 7, 2021 Category: Research Source Type: clinical trials

Tamoxifen Therapy for Myotubular Myopathy
Condition:   X Linked Myotubular Myopathy Interventions:   Drug: ApoTamox 10mg;   Drug: Placebo Sponsors:   James Dowling;   Canadian Institutes of Health Research (CIHR);   Cures Within Reach;   The Joshua Frase Foundation USA;   Will Cure USA;   Mogford Campbell Family Chair Fund Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 7, 2021 Category: Research Source Type: clinical trials

Early Phase Human Drug Trial to Investigate DYN101 in Participants 2 to 17 Years With Centronuclear Myopathies
Condition:   Centronuclear Myopathy Intervention:   Drug: DYN101 Sponsor:   Dynacure Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 8, 2021 Category: Research Source Type: clinical trials